03.07.24 -- The Future of Rare Diseases

Allogeneic cell therapies offer great clinical promise, but they also pose unique challenges. Consider these tips when looking for ways to make the translational journey easier.

Review the fundamentals of CRISPR technology, development, and its use to manipulate genes in different ways, such as altering their nucleotide sequences or changing their expression.

With the use of advanced in vitro models like organ-chips, researchers are gaining a better understanding of CAR T cell therapy in the context of solid tumors.

Adept CRO communication doesn’t just indicate the vendor’s ability to deliver a thoughtful bid; it demonstrates their ability to analyze, operationalize, and optimize a plan.

Gene delivery platforms must support a diversity of genetic engineering strategies for genomic medicine development. Learn how lipid nanoparticles can accelerate development from discovery to scale-up.

See how this Fortune 100 pharma company successfully addressed its HIV treatment research challenges through a partnership that provided a p24-expressing, non-infectious synthetic T cell mimic.

With each batch of cell and gene therapy product representing a wealth of lifesaving potential, this biopharma company needed the right packaging solution for its relatively new therapy applications.

As lentiviral vectors become more attractive options for CGT applications, sponsors need robust, efficient analytical platforms to accommodate upstream and downstream assessment.

Explore the growing field of cell and gene therapies along with a bioreactor system that is enabling researchers to expedite cell culture development and optimize their research time.

This demonstration examines an AAV upstream process in proprietary bioreactors, including an example of using process optimization to increase the fraction of full AAV capsids.

Learn about large and small volume parenteral injectable drugs, their comparative sizes, types, sterilization processes, and applications.