Newsletter | August 28, 2026

08.28.26 -- What Goes Into Restarting A Shelved Orphan Drug Candidate?

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The Cell & Gene Meeting on the Mesa is the sector’s premier annual conference, bringing together more than 1,500 industry leaders to address the key challenges facing cell and gene therapy commercialization. Featuring expert-led panels, extensive partnering opportunities, and 100+ company presentations, the meeting facilitates over 5,000 one-on-one meetings and showcases the latest clinical and commercial advances shaping the future of advanced therapies.

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What Goes Into Restarting A Shelved Orphan Drug Candidate?

A conversation between Elizabeth White of the Orphan Therapeutics Accelerator and Life Science Connect's Jon O'Connell

The Orphan Therapeutics Accelerator wants to help viable clinical-phase products reach patients. Its cofounder describes the complexity of rebooting a shelved candidate.

Polymer Technology Takes Freeze Containers Beyond The Breaking Point

Article | W.L. Gore & Associates

Learn about new materials being considered for single-use cold chain storage containers to reduce or eliminate issues with durability at cold temperatures.

SUPPLY CHAIN SOLUTIONS

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DEHP-Free Fluid Transfer Bags - Charter Medical

Assessing The Success Of CRISPR Gene Therapies Using ddPCR Technology

Application Note | By Marwan Alsarraj, Bio-Rad Laboratories, Inc.

Achieve high-fidelity results in gene therapy research. Discover how absolute quantification overcomes traditional limitations to provide the precision needed for validating CRISPR edits.

The Psychedelic Setback: What MDMA Rejection Taught Drug Developers

Article | Veristat, Inc.

Psychedelic compounds show real promise for PTSD, but proving its effectivity requires solving unblinding, bias, and safety gaps in trial design.

Decentralized And Community-Based Solutions Driving Women's Healthcare

White Paper | MRN - Medical Research Network

Clinical trials should reflect the affected population by reducing participation barriers and bringing trials to patients to increase inclusion and improve real-world data.

HRPP Vs IRB: How Unified Research Protections Empower Participants

Audio | Univo IRB

HRPPs and IRBs play different but connected roles in protecting research participants. Hear expert guidance, firsthand experiences, and questions that can help people make more informed decisions.

CLINICAL TRIALS SOLUTIONS

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Manage Your Clinical Trial Operations With This Platform - McCreadie Group

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