Successful Special Procedure Study Conduct: Cerebrospinal Fluid (CSF) And Concurrent Muscle Biopsy

Conducted in San Antonio, TX, this First-in-Human, Single Ascending Dose trial explored a novel therapeutic protein (TP) in 48 healthy volunteers. The study focused on cerebrospinal fluid (CSF) analysis to unveil the TP's pharmacokinetic profile and its binding at neuromuscular junctions. Worldwide helped the trial sponsor to successfully complete the study with full participant recruitment and retention, achieving comprehensive sampling and processing of all required matrices and time points.