Gene Therapy: Creative Solutions For Complex Clinical Development Pathways

Dedicated to making a difference.

Expertise in the rarest, most complex, and never done before novel therapies

Knowledge from nearly 600 rare disease programs and >100 cell and gene therapy programs.

Ensuring Patient Safety

Providing thoughtful clinical trial planning and conduct, navigating the regulatory approval process, and post-marketing safety surveillance.

Excellence in Scientific and Data-Driven Thinking

Integrated project teams offer critical thinking and calculated data-driven decisions throughout each step of your clinical development program.

We understand how high the stakes are with gene therapy programs. Nothing is standard about the study design, study conduct or regulatory process. Download our presentation from the 4th Annual Gene Therapy for Rare Disorders Meeting to learn about the manufacturing, clinical, and commercialization challenges drug developers face when bringing gene therapies to market.