Newsletter | February 13, 2026

02.13.26 -- Developing Itvisma For Broad-Range Treatment Of SMA With Dr. Norman Putzki

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FOCUS ON SUPPLY CHAIN

A New Container To Protect Bulk Frozen Biopharmaceuticals

Learn more about a freezer container that maintains package integrity after freezing at -86 °C (-123 °F) through its durable design, minimizing product loss due to package failure.

FOCUS ON CLINICAL TRIALS

Developing Itvisma For Broad-Range Treatment Of SMA With Dr. Norman Putzki

In episode 119 of Cell & Gene The Podcast, Host Erin Harris talks to Dr. Norman Putzki, Global Head Clinical Development, Novartis, about the development of and FDA approval of Itvisma, now the only gene replacement therapy approved for children, adolescents, and adults with spinal muscular atrophy (SMA).

Lost In Translation: Turning Multi-Omic Chaos Into Clinical Clarity

Uncover how this integrated, science-focused approach helps sponsors navigate biological complexity, streamline timelines, and make data-driven decisions across a collection of therapy programs.

The Need For Adaptive Distribution Partners For Cell And Gene Therapies

Optimize your commercial strategy by exploring how adaptive distribution models navigate reimbursement challenges and improve patient access. Partner early to align workflows and ensure operational success.

Developing Community-Based And Trial-Naïve Sites: The Real ROI

Trial-naïve sites, when supported with infrastructure, training, and network integration, represent a critical yet underused opportunity to expand patient access and accelerate recruitment.

CLINICAL TRIALS SOLUTIONS

Gain Objective Measures And Subjective Measures Of CNS Function - CHDR

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