Newsletter | March 14, 2025

03.14.25 -- Developing Bespoke Antisense Oligonucleotides To Treat Rare Diseases

SPONSOR

Webinar: Critical Imaging Risks in GLP-1 and Neurology Studies: What You Need to Know

Clinical trials in GLP-1 and neurology rely increasingly on imaging, but challenges often go unaddressed. This webinar covers early indicators of imaging issues, preclinical insights, expanding imaging requirements, and hidden risks. Attendees will learn how early identification of imaging risks, preclinical data, and strategic planning can mitigate delays, improve trial efficiency, and ensure regulatory compliance. Click here to learn more.

FOCUS ON SUPPLY CHAIN

4 Technologies Set To Transform The Pharma Supply Chain In 2025 And Beyond

These key technological advancements will significantly impact the pharma/biotech supply chain in 2025 and beyond. If you aren't implementing any of them yet, you may want to rethink your plans.

A Step-By-Step Guide To Cell Banking

Cell banking stands at the forefront of medical advancement. This guide delves into the steps involved in protecting these priceless resources, from cell collection and processing to storage and cell expansion.

Polymer Technology Takes Freeze Containers Beyond The Breaking Point

Learn about new materials being considered for single-use cold chain storage containers to reduce or eliminate issues with durability at cold temperatures.

FOCUS ON CLINICAL TRIALS

Developing Bespoke Antisense Oligonucleotides To Treat Rare Diseases

EveryONE Medicines CEO, Kent Rogers, explains the company’s mission to address a major unmet need in children with rare neurodegenerative diseases, one patient at a time.

Alzheimer's Trials: Replacing Reams Of Paper For LAR Consent

Explore a structured solution to automate the Legally Authorized Representative (LAR) workflow, ensuring that consent, reconsent, and assessments are accurately documented and compliant with regulations.

Expanding Patient Access To Cell And Gene Therapies

Rare disease innovation demands robust channel strategies for patient access. Learn how a patient-centric approach, logistical solutions, and strong partnerships are key to successful patient access.

Daring To Learn From Failure: The Future Of Stem Cell Therapy

Stem cell therapy has already revolutionized the field of oncology. But where do we go from here? Dr. Robert S. Negrin addresses three key areas of CAR T-cell therapy on the brink of innovation.

Connecting The Right Patients To The Right Trial

Direct outreach to potential participants and communication with their healthcare providers is key to boosting trial awareness and participation, thereby achieving recruitment targets.

Are You Leveraging All Of Your Clinical Data?

To develop and execute a successful clinical strategy, trial sponsors must be able to rapidly acquire detailed data insights. Learn how you can better utilize your trial data and achieve greater insights.

CLINICAL TRIALS SOLUTIONS

BioPharma Services: Data Licensing - Quest Diagnostics

Integrated Trial Services - MRN - Medical Research Network

The Global CRO For Biotechs - Avance Clinical

Addressing Site Selection Challenges In DMD Gene Therapy Studies - TFS HealthScience

Connect With Cell & Gene: