Newsletter | January 7, 2026

01.07.26 -- CSL's HEMGENIX Shows A New Future For Gene Therapy In Hemophilia B

FOCUS ON TRANSLATIONAL RESEARCH

CSL's HEMGENIX Shows A New Future For Gene Therapy In Hemophilia B

CSL's Dr. Deborah Long and Diego Sacristan highlight HEMGENIX's five-year Phase 3 data as a watershed for hemophilia B gene therapy.

Daring To Learn From Failure: The Future Of Stem Cell Therapy

Stem cell therapy has already revolutionized the field of oncology. But where do we go from here? Dr. Robert S. Negrin addresses three key areas of CAR T-cell therapy on the brink of innovation.

Measuring AAV Vector Genome Titer Using Droplet Digital PCR Protocol

Achieve highly consistent and precise AAV vector genome titer measurements with this optimized ddPCR protocol. This method ensures accurate dosing and optimal cell therapy potency.

Preserving Genomic Data's Living Legacy

Public genomic datasets like TCGA transformed cancer research, guiding assay validation and cohort design. Today, matched biospecimens complete the loop between digital insight and biological confirmation.

Development Of BCDP Reagents For 5' -Terminal Phosphate Oligonucleotides

New alternative phosphitylating reagents reduce the safety hazards associated with BCDP, enabling a safer and effective synthesis of key 5' -terminal phosphate oligonucleotide sequences.

Total Protein Stain Normalization Protocol

See how total protein staining offers a robust approach to western blot normalization to minimize variability and improve quantification accuracy, which supports reproducible protein expression.

Queen Mary University Of London's Centre For Predictive In Vitro Models

Discover the future of in vitro modeling at the Queen Mary+Emulate Organs-on-Chips Centre and unlock new possibilities in the field of predictive medicine.

Systematic Approach To Enhancing iPSC Expansion

Watch how to optimize iPSC culture conditions; transitioning to 3D stirred-tank bioreactors enables precise parameter control while maintaining high viability and essential stem cell characteristics.

Exploring Electroporation: Genetic Diseases

Innovative non-viral delivery methods are revolutionizing gene therapy by enabling precise, scalable genome editing in primary cells to address a wide spectrum of complex genetic disorders.

A Novel Patient-Derived Colorectal Cancer Organoid Platform

Patient-derived organoids are revolutionizing drug discovery by mimicking tumors to predict therapeutic efficacy. Uncover a scalable, reproducible, and cost-effective bioprocess that can pave the way for broader adoption.

TRANSLATIONAL RESEARCH SOLUTIONS

Immunoassays For Cytokine And Chemokine Quantitation - BD Biosciences

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